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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Clinical trials
Molecular docking
Animals
Muscle development
Immunoglobulin Fc Fragments/pharmacology
Allele‐specific silencing therapy
Humans
Myotendinous junction
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Génomique
Cell Line
Gene Expression Regulation/drug effects
Duchenne muscular dystrophy DMD
Gene modifiers
Muscle Biology
Genomic
Becker muscular dystrophy
DHPR α1S
Invivo
Muscles/physiopathology
Long noncoding RNA
DMO
Animal/physiopathology
Cachexia
Inhibitors
Becker muscular dystrophy BMD
Diseases
L-Type
Cultured
Homeostasis
Inbred mdx
Gene expression
Cardiomyopathy
Drp1
Becker BMD muscular dystrophy
CTNNB1
CD38
NNOS
MiARN
Epigenetics
Centronuclear myopathy
Dystrophin-EGFP
Myogenesis
DMD
Duchenne muscular dystrophy
BMD
LncARN
Knockout
Muscle
LKB1
Dystrophy
Male
Human Umbilical Vein Endothelial Cells
Hear
Skeletal muscle
Muscle Strength
Dystrophie Musculaire de Duchenne DMD
Dynamin 2
Dystrophie Musculaire de Becker BMD
Activin Receptors
CaVβs
MES
CaV subunits
Cardiomyopathie
Multi resolution modeling
Cells
Mitochondrial fission
Modificateurs de gènes
Hepatocellular carcinoma
Exon skipping
Antisense oligonucleotides
Muscular Atrophy
Ex-vivo
Dystrophie musculaire de Becker
Mdx mouse
Molecular Sequence Data
Dystrophin
Metabolism
Autophagy
Duchenne DMD dystrophy
Multi exon skipping
Cell homeostasis
Liver
Long QT
Muscular dystrophy
LncRNA
NAD+
Multiresolution modeling
Inbred C57BL
Delivery
Cell Biology
Morphogenesis
Dystrophine
Base Sequence
Energy Metabolism/drug effects
Calcium Channels
Calcium
Muscular Dystrophy
Dystrophin central domain
Mice